Compositions and methods for ttr gene editing and treating attr amyloidosis
Номер патента: EP3688161A1
Опубликовано: 05-08-2020
Автор(ы): Arti Mahendra Prakash Kanjolia, Jessica Lynn Seitzer, Reynald Michael Lescarbeau, Shobu ODATE, Walter Strapps
Принадлежит: Intellia Therapeutics Inc
Опубликовано: 05-08-2020
Автор(ы): Arti Mahendra Prakash Kanjolia, Jessica Lynn Seitzer, Reynald Michael Lescarbeau, Shobu ODATE, Walter Strapps
Принадлежит: Intellia Therapeutics Inc
Реферат: Compositions and methods for editing, e.g., introducing double-stranded breaks, within the TTR gene are provided. Compositions and methods for treating subjects having amyloidosis associated with transthyretin (ATTR), are provided.
compositions and methods for editing the ttr gene and treating attr amyloidosis
Номер патента: BR112020005287A2. Автор: Walter Strapps,Shobu ODATE,Arti Mahendra Prakash Kanjolia,Jessica Lynn Seitzer,Reynald Michael Lescarbeau. Владелец: Intellia Therapeutics, Inc.. Дата публикации: 2020-09-24.