Compound and method for an allele-specific editing of the elane gene
Номер патента: EP4367240A1
Опубликовано: 15-05-2024
Автор(ы): Julia Skokowa, Masoud Nasri, Perihan Mir
Принадлежит: EBERHARD KARLS UNIVERSITAET TUEBINGEN, Universitaetsklinikum Tuebingen
Опубликовано: 15-05-2024
Автор(ы): Julia Skokowa, Masoud Nasri, Perihan Mir
Принадлежит: EBERHARD KARLS UNIVERSITAET TUEBINGEN, Universitaetsklinikum Tuebingen
Реферат: The present invention relates to a nucleic acid molecule for an allele-specific editing of the ELANE gene, a vector comprising said nucleic acid molecule, a composition comprising said nucleic acid molecule or vector, a method in vitro for an allele-specific editing the ELENE gene in biological material including genetic material encoding said ELENE gene, and to a method for the prophylaxis and/or treatment and/or examination of a disease in a living being.
Compound and method for an allele-specific editing of the elane gene
Номер патента: EP4116418A1. Автор: Julia Skokowa,Masoud Nasri,Perihan Mir. Владелец: Universitaetsklinikum Tuebingen. Дата публикации: 2023-01-11.